List of orphan drugs

1. A list of all orphan drugs was downloaded from the FDA s Orphan Drug Designations and Approvals database (FDAOD) website . The start date was set to default to to the end date of . The spreadsheet was downloaded on . The list downloaded from the FDAOD consisted of 1033 approvals for orphan-designated drugs.

This series includes a list of rare diseases, reports on epidemiological data, list of orphan drugs, rare disease registries in Europe, list of research

Trends of orphan drugs in the WHO Essential Medicines List 2024 - 2024. Page 7. The contribution of FDA and EMA's orphan drugs to fuelling the EML (ATC level).

Covered entities and their partners may need to analyze drugs on the OOPD list to decide which orphan drugs to exclude from the 340B Program and the appropriate time frame. We encourage 340B stakeholders to resolve any potential disputes on access to orphan drugs. How to use the OOPD database to create a list of currently designated orphan drug

44 The FDA updates a publicly available list of orphan designations every month.45. FDA may revoke an orphan-drug designation after it is

by 刘鑫 2024 Cited by 6From the the first list of rare diseases, there are 60 orphan drugs for 36 diseases in the US and 27 orphan drugs for 18 diseases in the EU, and the orphan

orphan drugs after obtaining orphan drug designations. Page 9. 9 The list of incentives of orphan drug designation include: ▫ Pre

Lists of medicinal Products for Rare diseases in Europe; Orphan Drugs Collection. January 2024. 4. Orphan Drug Designations and Approvals List as of 03- 03

This series includes a list of rare diseases, reports on epidemiological data, list of orphan drugs, rare disease registries in Europe, list of research